Aiza becomes the first foreign child successfully treated with Chinese-developed CS-101 gene therapy A groundbreaking milestone in gene therapy has been achieved as a 4-year-old Pakistani girl named Aiza has been cured…
Tag: thalassemia treatement
β-Thalassemia Major Complicated by Acute Myeloid Leukemia: A Case Report
AbstractThis report presents a rare case of a 4.5-year-old boy with β-thalassemia major, who developed acute myeloid leukemia (AML) French-American-British type M2. β-thalassemia major is an inherited hemoglobinopathy characterized by severe, transfusion-dependent…
