Pioneering gene therapy rescues US baby from uncommon liver disease
Groundbreaking Gene Editing Therapy Saves Infant’s Life In a remarkable medical achievement, an infant in the United States suffering from a rare genetic disorder has […]
Tag: genetic disorder
FDA Approves First-Ever Treatment for Cerebrotendinous Xanthomatosis (CTX)
In a significant milestone for the medical community, the U.S. Food and Drug Administration (FDA) has granted approval for the first-ever treatment for Cerebrotendinous Xanthomatosis […]
